Multiple Choice
Which of the following would provide the longest lasting treatment for adenosine deaminase (ADA) deficiency?
A) injecting PEG-ADA purified from a cow
B) injecting white blood cells genetically modified to carry functional ADA genes
C) supplying progenitor T cells genetically modified to carry functional ADA genes shortly after birth
D) using siRNA to knockdown ADA genes
E) using cDNA to produce ADA in E. coli
Correct Answer:
Verified
Correct Answer:
Verified
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